Buscar resultados de ensayos clínicos
Familial Transthyretin Amyloidosis - 25 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: Safety, Efficacy and Pharmacokinetics of Doxycycline Plus Tauroursodeoxycholic Acid in Transthyretin Amyloidosis Condición: Transthyretin Amyloidosis Fecha: 2010-07-27 Intervenciones: Drug: Doxycycline + Tauroursodeoxycholic acid doxycycline 100 mg twice a day for 12 months; tauroursodeo |
Completed |
Nombre del estudio: Study of SOM0226 in Familial Amyloid Polyneuropathy Condición: Familial Amyloid Polyneuropathy (FAP) Fecha: 2014-07-09 Intervenciones: Drug: SOM0226 Oral |
Completed |
Nombre del estudio: The Effect Of Tafamidis For The Transthyretin Amyloid Polyneuropathy Patients With V30M Or Non-V30M Transthyretin Condición: Transthyretin Familial Amyloid Polyneuropathy Fecha: 2011-09-13 Intervenciones: Drug: tafamidis tafamidis meglumine 20 mg QD Other N |
Completed |
Nombre del estudio: An Extension of Study Fx-005 Evaluating Long-Term Safety And Clinical Outcomes Of Fx-1006A In Patients With Transthyretin Amyloid Polyneuropathy Condición:
Fecha: 2008-11-13 Intervenciones: Drug: Fx-1006A Fx-1006A 20mg soft gelatin capsule administered orally once daily (at the same time each |
Completed |
Nombre del estudio: Safety and Efficacy Study of Fx-1006A in Patients With Familial Amyloidosis Condición: Familial Amyloid Polyneuropathy Fecha: 2006-12-06 Intervenciones:
|
Completed |
Nombre del estudio: The Effect of Diflunisal on Familial Transthyretin Amyloidosis Condición: Amyloidosis Fecha: 2011-09-09 Intervenciones: Drug: Diflunisal Film-coated tablet, 250 mg twice daily, orally for approximately 2 years |
Active, not recruiting |
Nombre del estudio: Efficacy and Safety of IONIS-TTR Rx in Familial Amyloid Polyneuropathy Condición:
|
Enrolling by invitation |
Nombre del estudio: Open-Label Extension Assessing Long Term Safety and Efficacy of IONIS-TTR Rx in Familial Amyloid Polyneuropathy (FAP) Condición:
|
Recruiting |
Nombre del estudio: Transthyretin-Associated Amyloidoses Outcome Survey (THAOS) Condición:
Fecha: 2008-02-25 Intervenciones: Other: None. Observational Study. |